Applications of Gene Editing

TECHNOLOGICAL ADVANCES & APPLICATIONS IN GENOME EDITING

Enabling more Precise and Efficacious Genome Editing & Quantifying its Outcomes

• Get to grips with the repurposing of CRISPR-Cas 9 and all its variants  
• Exchange ideas on tools for on and off target effects when using different enzymes & variants
• Understanding on-target cutting – analyzing events at the intended site

Delivery, Administration & Editing Applications for Genetic Disease

• Become an expert on non-viral delivery methods including nano injection, nanoparticles and more…
• Simplify in vivo approaches to eye disease & DMD treatment
• Discuss CRISPR and potential treatment strategies in blood and liver disorders

Novel Gene Editing Applications in CART

• Understand next generations technologies in adoptive T cell immunotherapy
• Prepare for allo CAR & T Cell Therapies – iPSc, Gene editing & highly characterized products
• Build controls for product quality & specifications around gene editing